Drug Development

Illustration of the neuromuscular junction, where nerves send signals to muscles.
Featured Article

Understanding Congenital Myasthenic Syndrome: Causes and Treatments

By Justine Savage | May 23, 2025
Illustration of a researcher in a white lab coat climbing a ladder shaped like a DNA helix.
Featured Article

Why MDA’s Kickstart Program Is a Game-changer for Gene Therapies

By Amy Bernstein | May 23, 2025
Blog Post

Celebrating 25 Years of Impact: MDA’s Wings Over Wall Street Gala Honors Leaders in ALS Research and Advocacy

By MDA Staff | March 16, 2025
Blog Post

Quest Podcast: PJ’s Protocol: A Lifesaving Procedure Fueled by Love

By MDA Staff | March 6, 2025
Composite image of scientific lab instruments: a microscope, a pipette, petri dishes, and a computer keyboard.
Featured Article

Innovations in GNE Myopathy Research

By Amy Bernstein | February 28, 2025
Creatine kinase (CK), also known as creatine phosphokinase (CPK) or phosphocreatine kinase, is an enzyme expressed by various tissues and cell types. CK catalyses the conversion of creatine and uses adenosine triphosphate (ATP) to create phosphocreatine (PCr) and adenosine diphosphate (ADP). This CK enzyme reaction is reversible and thus ATP can be generated from PCr and ADP.
Blog Post

Simply Stated: RNA-Based Therapies in Development for Myotonic Dystrophy

By Sujatha Gurunathan | January 30, 2025
A researcher in a white lab coat with long brown hair rests her chin on her hand next to a computer with science research on the screen
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Innovative Research: Spotlight on MDA Research Grant Recipients

By Larry Luxner | December 20, 2024
Medical Research Scientist Working on Desktop Computer with Gene Analysis Software in Modern Science Research Laboratory. Lab Engineers in White Coats Conduct Experiments in the Background.
Blog Post

Simply Stated: Emerging Therapies to Treat DMD

By Sujatha Gurunathan | December 20, 2024
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In Case You Missed It…

By MDA Staff | December 8, 2024
A young boy in a batman t shirt holds up a sign that says HOPE in front of a red curtain
Blog Post

MDA CEO and President Dr. Wood Reflects on 2024: A Year of Milestones and Momentum

By Donald S. Wood, Ph.D., President and CEO, Muscular Dystrophy Association | December 5, 2024